affairs plans for various gene therapies, including within the inborn errors of metabolism therapeutic area. Furthermore, the... to develop gene therapies for patients with rare and ultra-rare diseases. Reporting to the Sr. Director, Global Medical Affairs...
and US Field Medical team across the Inborn Errors of Metabolism (IEM) portfolio to ensure execution of medical plans by leading... gene therapy portfolio, initially focused on Inborn Errors of Metabolism. The company is launching over the next 2 years...